SUSTAINED MUTANT HUNTINGTIN LOWERING IN THE BRAIN AND CEREBROSPINAL FLUID OF HUNTINGTON DISEASE MINIPIGS MEDIATED BY AAV5-MIHTT GENE THERAPY

Vallés, A., Brouwers, C., Pintauro, R., Snapper, J., Bohuslavová, B., Sogorb-Gonzales, M., Fodale, V., Bresciani, A., Ellederová, Z., Blits, B., Motlík, J., van Deventer, S., Evers, M., Konstantinová, P. SUSTAINED MUTANT HUNTINGTIN LOWERING IN THE BRAIN AND CEREBROSPINAL FLUID OF HUNTINGTON DISEASE MINIPIGS MEDIATED BY AAV5-MIHTT GENE THERAPY. Journal of Neurology Neurosurgery and Psychiatry. 2018, 89(S1), A89-A90. ISSN 0022-3050. E-ISSN 1468-330X. Dostupné z: doi: 10.1136/jnnp-2018-EHDN.241