SUSTAINED MUTANT HUNTINGTIN LOWERING IN THE BRAIN AND CEREBROSPINAL FLUID OF HUNTINGTON DISEASE MINIPIGS MEDIATED BY AAV5-MIHTT GENE THERAPY

VALLÉS, A., BROUWERS, C., PINTAURO, R., SNAPPER, J., BOHUSLAVOVÁ, B., SOGORB-GONZALES, M., FODALE, V., BRESCIANI, A., ELLEDEROVÁ, Z., BLITS, B., MOTLÍK, J., VAN DEVENTER, S., EVERS, M., KONSTANTINOVÁ, P. SUSTAINED MUTANT HUNTINGTIN LOWERING IN THE BRAIN AND CEREBROSPINAL FLUID OF HUNTINGTON DISEASE MINIPIGS MEDIATED BY AAV5-MIHTT GENE THERAPY. Journal of Neurology Neurosurgery and Psychiatry. 2018, 89(S1), A89-A90. ISSN 0022-3050. E-ISSN 1468-330X. Dostupné z: doi: 10.1136/jnnp-2018-EHDN.241