0498974 - ÚŽFG 2019 RIV GB eng A - Abstract
Klíma, Jiří - Evers, M. - Miniariková, J. - Juhás, Štefan - Vallés, A. - Bohuslavová, Božena - Juhásová, Jana - Kupcová Skalníková, Helena - Vodička, Petr - Valeková, Ivona - Brouwers, C. - Blits, B. - Lubelski, J. - Kovářová, Hana - van Deventer, S. - Petry, H. - Motlík, Jan - Konstantinová, P. - Ellederová, Zdeňka
AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL.
Journal of Neurology Neurosurgery and Psychiatry. Roč. 89, S1 (2018), A89-A89. ISSN 0022-3050. E-ISSN 1468-330X.
[Plenary Meeting of the European Huntington´s Disease Network (EHDN). 14.09.2018-16.09.2018, Vienna]
R&D Projects: GA MŠMT(CZ) LO1609
Institutional support: RVO:67985904
Keywords : AAV5-MHTT gene therapy * Huntingtonˇs disease
OECD category: Genetics and heredity (medical genetics to be 3)
DOI: https://doi.org/10.1136/jnnp-2018-EHDN.240
Permanent Link: http://hdl.handle.net/11104/0291258
Klíma, Jiří - Evers, M. - Miniariková, J. - Juhás, Štefan - Vallés, A. - Bohuslavová, Božena - Juhásová, Jana - Kupcová Skalníková, Helena - Vodička, Petr - Valeková, Ivona - Brouwers, C. - Blits, B. - Lubelski, J. - Kovářová, Hana - van Deventer, S. - Petry, H. - Motlík, Jan - Konstantinová, P. - Ellederová, Zdeňka
AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL.
Journal of Neurology Neurosurgery and Psychiatry. Roč. 89, S1 (2018), A89-A89. ISSN 0022-3050. E-ISSN 1468-330X.
[Plenary Meeting of the European Huntington´s Disease Network (EHDN). 14.09.2018-16.09.2018, Vienna]
R&D Projects: GA MŠMT(CZ) LO1609
Institutional support: RVO:67985904
Keywords : AAV5-MHTT gene therapy * Huntingtonˇs disease
OECD category: Genetics and heredity (medical genetics to be 3)
DOI: https://doi.org/10.1136/jnnp-2018-EHDN.240
Permanent Link: http://hdl.handle.net/11104/0291258