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AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington's Disease Minipig Model
- 1.EVERS, M., MINIARIKOVA, J., JUHÁS, Štefan, VALLÉS, A., BOHUSLAVOVÁ, Božena, JUHÁSOVÁ, Jana, KUPCOVÁ SKALNÍKOVÁ, Helena, VODIČKA, Petr, VALEKOVÁ, Ivona, BROUWERS, C., BLITS, B., LUBELSKI, J., KOVÁŘOVÁ, Hana, ELLEDEROVÁ, Zdeňka, VAN DEVENTER, S., PETRY, H., MOTLÍK, Jan, KONSTANTINOVÁ, P. AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington's Disease Minipig Model. Molecular Therapy. 2018, 26(9), 2163-2177. ISSN 1525-0016. E-ISSN 1525-0024. Available: https://doi.org/10.1016/j.ymthe.2018.06.021
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