- AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HU…
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AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL

  1. 1.
    SYSNO0498974
    TitleAAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL
    Author(s) Klíma, Jiří (UZFG-Y) [LBRP] RID, ORCID
    Evers, M. (NL)
    Miniariková, J. (US)
    Juhás, Štefan (UZFG-Y) [LBRP] RID, ORCID
    Vallés, A. (NL)
    Bohuslavová, Božena (UZFG-Y) [LBRP] ORCID
    Juhásová, Jana (UZFG-Y) [LBRP] RID, ORCID
    Kupcová Skalníková, Helena (UZFG-Y) [LAPA] RID, ORCID
    Vodička, Petr (UZFG-Y) [LAPA] ORCID
    Valeková, Ivona (UZFG-Y) [LBRP] RID, ORCID
    Brouwers, C. (NL)
    Blits, B. (NL)
    Lubelski, J. (NL)
    Kovářová, Hana (UZFG-Y) [LAPA] RID, ORCID
    van Deventer, S. (NL)
    Petry, H. (NL)
    Motlík, Jan (UZFG-Y) [LBRP] RID, ORCID
    Konstantinová, P. (NL)
    Ellederová, Zdeňka (UZFG-Y) [LBRP] RID, ORCID
    Source Title Journal of Neurology Neurosurgery and Psychiatry. Roč. 89, S1 (2018), A89-A89
    Conference Plenary Meeting of the European Huntington´s Disease Network (EHDN), 14.09.2018 - 16.09.2018, Vienna
    Document TypeAbstrakt
    Grant LO1609 GA MŠMT - Ministry of Education, Youth and Sports (MEYS), CZ - Czech Republic
    Institutional supportUZFG-Y - RVO:67985904
    Languageeng
    CountryGB
    Keywords AAV5-MHTT gene therapy * Huntingtonˇs disease
    Permanent Linkhttp://hdl.handle.net/11104/0291258
     
Number of the records: 1  

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