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Nanoparticle mediated non-viral CRISPR/Cas gene editing transfer system for retinal gene therapy
- 1.Rohiwal, S. S., Klíma, J., Vaškovičová, M., Šlouf, M., Pavlová, E., Štěpánek, P., Bogomolova, A., Ellederová, Z., Stieger, K. Nanoparticle mediated non-viral CRISPR/Cas gene editing transfer system for retinal gene therapy. In: The 4th Animal Models of Neurodegenerative Diseases. Liběchov: ÚŽFG AV ČR, v. v. i., 2017, s. 41-41.
Number of the records: 1