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  1. 1.
    0498974 - ÚŽFG 2019 RIV GB eng A - Abstract
    Klíma, Jiří - Evers, M. - Miniariková, J. - Juhás, Štefan - Vallés, A. - Bohuslavová, Božena - Juhásová, Jana - Kupcová Skalníková, Helena - Vodička, Petr - Valeková, Ivona - Brouwers, C. - Blits, B. - Lubelski, J. - Kovářová, Hana - van Deventer, S. - Petry, H. - Motlík, Jan - Konstantinová, P. - Ellederová, Zdeňka
    AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL.
    Journal of Neurology Neurosurgery and Psychiatry. Roč. 89, S1 (2018), A89-A89. ISSN 0022-3050. E-ISSN 1468-330X.
    [Plenary Meeting of the European Huntington´s Disease Network (EHDN). 14.09.2018-16.09.2018, Vienna]
    R&D Projects: GA MŠMT(CZ) LO1609
    Institutional support: RVO:67985904
    Keywords : AAV5-MHTT gene therapy * Huntingtonˇs disease
    OECD category: Genetics and heredity (medical genetics to be 3)
    Permanent Link: http://hdl.handle.net/11104/0291258
     
     

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